Toward a Gene Therapy for Dominant Disease: Validation of an RNA Interference-Based Mutation-Independent Approach
Titel:
Toward a Gene Therapy for Dominant Disease: Validation of an RNA Interference-Based Mutation-Independent Approach
Auteur:
Kiang, Anna-Sophia Palfi, Arpad Ader, Marius Kenna, Paul F. Millington-Ward, Sophia Clark, Gerry Kennan, Avril O'Reilly, Mary Tam, Lawrence C.T. Aherne, Aileen McNally, Niamh Humphries, Pete Farrar, G. Jane