Replacing acid α-glucosidase in Pompe disease: recombinant and transgenic enzymes are equipotent, but neither completely clears glycogen from type II muscle fibers
Titel:
Replacing acid α-glucosidase in Pompe disease: recombinant and transgenic enzymes are equipotent, but neither completely clears glycogen from type II muscle fibers
Auteur:
Raben, Nina Fukuda, Tokiko Gilbert, Abigail L. de Jong, Deborah Thurberg, Beth L. Mattaliano, Robert J. Meikle, Peter Hopwood, John J. Nagashima, Kunio Nagaraju, Kanneboyina Plotz, Paul H.