Long-Term Correction of Ornithine Transcarbamylase Deficiency by WPRE-Mediated Overexpression Using a Helper-Dependent Adenovirus
Title:
Long-Term Correction of Ornithine Transcarbamylase Deficiency by WPRE-Mediated Overexpression Using a Helper-Dependent Adenovirus
Author:
Mian, Asad McCormack Jr., W.Michael Mane, Viraj Kleppe, Soledad Ng, Philip Finegold, Milton O'Brien, William E. Rodgers, John R. Beaudet, Arthur L. Lee, Brendan