100. A multicentre retrospective survey of miglustat in patients with Niemann-Pick type C disease
Title:
100. A multicentre retrospective survey of miglustat in patients with Niemann-Pick type C disease
Author:
Patterson, Marc Pineda, Merci Sedel, Fridiric Mengel, Eugen Hwu, Wuh-Liang Rohrbach, Marianne Bembi, Brubo Korenke, Christoph Luzy, Cicile Schieber, Peter Giorgino, Ruben Wraith, Ed