A dose-optimization trial of laronidase (Aldurazyme®) in patients with mucopolysaccharidosis I
Titel:
A dose-optimization trial of laronidase (Aldurazyme®) in patients with mucopolysaccharidosis I
Auteur:
Giugliani, Roberto Rojas, Verónica Muñoz Martins, Ana Maria Valadares, Eugênia R. Clarke, Joe T.R. Góes, José E.C. Kakkis, Emil D. Worden, Mary Alice Sidman, Marisa Cox, Gerald F.