Cipaglucosidase alfa/miglustat versus alglucosidase alfa/placebo in late-onset Pompe disease (LOPD): PROPEL study subgroup analyses
Title:
Cipaglucosidase alfa/miglustat versus alglucosidase alfa/placebo in late-onset Pompe disease (LOPD): PROPEL study subgroup analyses
Author:
Byrne, Barry Bratkovic, Drago Díaz-Manera, Jordi Laforêt, Pascal Mozaffar, Tahseen van der Ploeg, Ans Roberts, Mark Schoser, Benedikt Toscano, Antonio Jiang, Hai Sitaraman, Sheela Goldman, Mitchell Castelli, Jeff Kishnani, Priya S.