Baby-COMET methodology: A clinical study of the efficacy, safety, pharmacokinetics, and pharmacodynamics of avalglucosidase alfa in treatment-naïve participants with IOPD
Titel:
Baby-COMET methodology: A clinical study of the efficacy, safety, pharmacokinetics, and pharmacodynamics of avalglucosidase alfa in treatment-naïve participants with IOPD
Auteur:
Broomfield, Alexander Davison, James Donati, Maria Alice Haack, Kristina An Tammireddy, Swathi Thibault, Nathan Woloschak, Michael Zaher, Atef Zhou, Tianyue Hahn, Andreas