Farber disease clinical impact: Patient reported outcomes as a measure of disease burden
Title:
Farber disease clinical impact: Patient reported outcomes as a measure of disease burden
Author:
Mitchell, John Harmatz, Paul Selim, Laila Din, Iman Gamal El Mungan, Neslihan Bulut, Fatma Lampe, Christina Grant, Christina L. Ferreira, Carlos R. Puri, Ratna D. Bijarnia-Mahay, Sunita Arslan, Nur Guelbert, Norberto Zaki, Maha S. Kapoor, Seema Hahn, Andreas Magnusson, Bo Sundberg, Erik Ozen, Seza Batu, Ezgi D. Di Rocco, Maja Gokcay, Gulden Crosby, Kathleen Solyom, Alexander