Exploration of the efficacy of pabinafusp-alfa (JR-141) on neurocognitive development in Hunter syndrome (MPS II): 52-week data from clinical trials in Japan and Brazil
Titel:
Exploration of the efficacy of pabinafusp-alfa (JR-141) on neurocognitive development in Hunter syndrome (MPS II): 52-week data from clinical trials in Japan and Brazil
Auteur:
Giugliani, Roberto Martins, Ana Maria Okuyama, Torayuki Eto, Yoshikatsu Sakai, Norio Nakamura, Kimitoshi So, Sairei Yamamoto, Tatsuyoshi Yamaoka, Mariko Ikeda, Toshiaki Tanizawa, Kazunori Sonoda, Hiroyuki Schmidt, Mathias Sato, Yuji