Comparison of cognitive function in siblings with neuronopathic mucopolysaccharidosis type II: Evaluation of early treatment with intravenous idursulfase and intrathecal idursulfase-IT
Titel:
Comparison of cognitive function in siblings with neuronopathic mucopolysaccharidosis type II: Evaluation of early treatment with intravenous idursulfase and intrathecal idursulfase-IT
Auteur:
Muenzer, Joseph Burton, Barbara K. Harmatz, Paul Gutiérrez-Solana, Luis González Ruiz-Garcia, Matilde Jones, Simon A. Guffon, Nathalie Inbar-Feigenberg, Michal Bratkovic, Drago Li, Xiaoxi Yee, Karen S. Alexanderian, David