The RETRIEVE Study: A natural history study of type 2 Gaucher disease, and GM1 and GM2 gangliosidoses with early onset, in preparation of a clinical trial
Title:
The RETRIEVE Study: A natural history study of type 2 Gaucher disease, and GM1 and GM2 gangliosidoses with early onset, in preparation of a clinical trial
Author:
Heron-Longe, Benedicte Batzios, Spyros Mengel, Eugen Giugliani, Roberto Patterson, Marc Gautschi, Matthias Alcantara, Jose Cornelisse, Peter Trokan, Luba Schwierin, Barbara Rohrbach, Marianne