Mini-COMET study: Individual participant-level responses to treatment in patients with infantile-onset Pompe disease receiving repeated dose regimens of avalglucosidase alfa or alglucosidase alfa who were previously treated with alglucosidase alfa
Title:
Mini-COMET study: Individual participant-level responses to treatment in patients with infantile-onset Pompe disease receiving repeated dose regimens of avalglucosidase alfa or alglucosidase alfa who were previously treated with alglucosidase alfa
Author:
Kishnani, Priya S. Brassier, Anaïs Broomfield, Alexander Davison, James Hahn, Si Houn Kumada, Satoko Labarthe, François Ohki, Hirotaka Pichard, Samia Haack, Kristina An Johnson, Judith Meng, Xianzhang Chien, Yin-Hsiu Kronn, David