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FLT201: An AAV-mediated gene therapy for type 1 Gaucher disease designed to target difficult to reach tissues |
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Title: |
FLT201: An AAV-mediated gene therapy for type 1 Gaucher disease designed to target difficult to reach tissues |
Author: |
Corbau, Romuald Miranda, Carlos Comper, Fabrizio Kalcheva, Petya Chisari, Elisa Cocita, Clement Correia, Samantha Pandya, Jalpa Liou, Benjamin Northcott, Natalie Stotter, Emmaline Shehu, Erald Yu, I-Mei Khinder, Jaminder Sheridan, Rose Sun, Ying Nathwani, Amit |
Appeared in: |
Molecular genetics and metabolism |
Paging: |
Volume 132 () nr. 2 pages S28-S29 |
Year: |
2021 |
Contents: |
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Publisher: |
Published by Elsevier B.V. |
Source file: |
Elektronische Wetenschappelijke Tijdschriften |
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