Glycerol phenylbutyrate treatment in children with urea cycle disorders: Pooled analysis of short and long-term ammonia control and outcomes
Title:
Glycerol phenylbutyrate treatment in children with urea cycle disorders: Pooled analysis of short and long-term ammonia control and outcomes
Author:
Berry, Susan A. Lichter-Konecki, Uta Diaz, George A. McCandless, Shawn E. Rhead, William Smith, Wendy LeMons, Cynthia Nagamani, Sandesh C.S. Coakley, Dion F. Mokhtarani, Masoud Scharschmidt, Bruce F. Lee, Brendan