A randomised, placebo-controlled, phase III trial of leniolisib in activated phosphoinositide 3-kinase delta (PI3Kδ) syndrome (APDS): Adolescent and adult subgroup analysis
Titel:
A randomised, placebo-controlled, phase III trial of leniolisib in activated phosphoinositide 3-kinase delta (PI3Kδ) syndrome (APDS): Adolescent and adult subgroup analysis
Auteur:
Rao, V. Koneti Šedivá, Anna Dalm, Virgil A.S.H. Plebani, Alessandro Schuetz, Catharina Shcherbina, Anna Trizzino, Antonino Zharankova, Yulia Orpia, Alanvin Kulm, Elaine Webster, Sharon Körholz, Julia Lougaris, Vassilios Rodina, Yulia Conlon, Niall Coulter, Tanya Bradt, Jason Relan, Anurag Uzel, Gulbu