20 Multi-Year Registry Study of Elapegademase-lvlr Treatment in Patients with Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID) Requiring Enzyme Replacement Therapy (ERT)
Title:
20 Multi-Year Registry Study of Elapegademase-lvlr Treatment in Patients with Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID) Requiring Enzyme Replacement Therapy (ERT)
Author:
Dorsey, Morna Butte, Manish Lieberman, Jay Lehman, Heather Fausnight, Tracy Keller, Michael Fradette, Caroline Hershfield, Michael Pozos, Tamara Rozova, Anna Wall, Luke Morena, M. Teresa de la Bednarski, Jeffrey Tarrant, Teresa Chong, Hey Geng, Bob Temin, Noemi Toiber Laubach, Susan Lin, Leo Mousallem, Talal Walter, Jolan