RAG deficiency with ALPS features successfully treated with TCRαβ/CD19 cell depleted haploidentical stem cell transplant
Titel:
RAG deficiency with ALPS features successfully treated with TCRαβ/CD19 cell depleted haploidentical stem cell transplant
Auteur:
Westermann-Clark, Emma Grossi, Alice Fioredda, Francesca Giardino, Stefano Cappelli, Enrico Terranova, Paola Palmisani, Elena Farmer, Jocelyn R. Foldvari, Zsofia Yamazaki, Yasuhiro Faraci, Maura Lanino, Edoardo Notarangelo, Luigi D. Dufour, Carlo Ceccherini, Isabella Walter, Jolan E. Miano, Maurizio