Management goals for type 1 Gaucher disease: An expert consensus document from the European working group on Gaucher disease
Titel:
Management goals for type 1 Gaucher disease: An expert consensus document from the European working group on Gaucher disease
Auteur:
Biegstraaten, M. Cox, T.M. Belmatoug, N. Berger, M.G. Collin-Histed, T. Vom Dahl, S. Di Rocco, M. Fraga, C. Giona, F. Giraldo, P. Hasanhodzic, M. Hughes, D.A. Iversen, P.O. Kiewiet, A.I. Lukina, E. Machaczka, M. Marinakis, T. Mengel, E. Pastores, G.M. Plöckinger, U. Rosenbaum, H. Serratrice, C. Symeonidis, A. Szer, J. Timmerman, J. Tylki-Szymańska, A. Weisz Hubshman, M. Zafeiriou, D.I. Zimran, A. Hollak, C.E.M.