Sinbaglustat ameliorates disease pathology in a murine model of GM1 gangliosidosis without affecting CNS ganglioside levels
Titel:
Sinbaglustat ameliorates disease pathology in a murine model of GM1 gangliosidosis without affecting CNS ganglioside levels
Auteur:
Wannemacher, Rouven Jubran-Rudolf, Lorna Zdora, Isabel Leitzen, Eva Rohn, Karl Sippel, Virginie Paschen, Christoph Blattmann, Peter Baumgärtner, Wolfgang Gerhauser, Ingo Steiner, Michel Alexander