Rescue of gene-expression changes in an induced mouse model of spinal muscular atrophy by an antisense oligonucleotide that promotes inclusion of SMN2 exon 7
Titel:
Rescue of gene-expression changes in an induced mouse model of spinal muscular atrophy by an antisense oligonucleotide that promotes inclusion of SMN2 exon 7
Auteur:
Staropoli, John F. Li, Huo Chun, Seung J. Allaire, Norm Cullen, Patrick Thai, Alice Fleet, Christina M. Hua, Yimin Bennett, C. Frank Krainer, Adrian R. Kerr, Doug McCampbell, Alexander Rigo, Frank Carulli, John P.