Intravitreal enzyme replacement preserves retinal structure and function in canine CLN2 neuronal ceroid lipofuscinosis
Titel:
Intravitreal enzyme replacement preserves retinal structure and function in canine CLN2 neuronal ceroid lipofuscinosis
Auteur:
Whiting, Rebecca E.H. Pearce, Jacqueline W. Vansteenkiste, Daniella P. Bibi, Katherine Lim, Stefanie Robinson Kick, Grace Castaner, Leilani J. Sinclair, John Chandra, Sundeep Nguyen, Annalisa O'Neill, Charles A. Katz, Martin L.