Intravitreal implantation of TPP1-transduced stem cells delays retinal degeneration in canine CLN2 neuronal ceroid lipofuscinosis
Titel:
Intravitreal implantation of TPP1-transduced stem cells delays retinal degeneration in canine CLN2 neuronal ceroid lipofuscinosis
Auteur:
Tracy, Christopher J. Whiting, Rebecca E.H. Pearce, Jacqueline W. Williamson, Baye G. Vansteenkiste, Daniella P. Gillespie, Lauren E. Castaner, Leilani J. Bryan, Jeffrey N. Coates, Joan R. Jensen, Cheryl A. Katz, Martin L.