The Mini-COMET Clinical Trial: Safety and Efficacy of Avalglucosidase Alfa after 97 Weeks of Treatment in Children with Infantile-Onset Pompe Disease Previously Treated with Alglucosidase Alfa
Titel:
The Mini-COMET Clinical Trial: Safety and Efficacy of Avalglucosidase Alfa after 97 Weeks of Treatment in Children with Infantile-Onset Pompe Disease Previously Treated with Alglucosidase Alfa
Auteur:
Kronn, David Davison, James Broomfield, Alexander Brassier, Anaïs Labarthe, François Hahn, Si Houn Kumada, Satoko Ohki, Hirotaka Prakalapakorn, Sasapin Grace Wilson, Catherine Haack, Kristina An Huynh-ba, Olivier Richards, Susan Sparks, Susan Tammireddy, Swathi Zhou, Tianyue Chien, Yin-Hsiu Kishnani, Priya S.