Evidence of Treatment Benefits in Patients with Mucopolysaccharidosis Type I-Hurler in Long-term Follow-up Using a New Magnetic Resonance Imaging Scoring System
Titel:
Evidence of Treatment Benefits in Patients with Mucopolysaccharidosis Type I-Hurler in Long-term Follow-up Using a New Magnetic Resonance Imaging Scoring System
Auteur:
Pontesilli, Silvia Baldoli, Cristina Rosa, Pasquale Anthony Della Cattoni, Alessandro Bernardo, Maria Ester Meregalli, Pamela Gasperini, Serena Motta, Serena Fumagalli, Francesca Tucci, Francesca Baciga, Federica Consiglieri, Giulia Canonico, Francesco De Lorenzo, Paola Chiapparini, Luisa Gentner, Bernhard Aiuti, Alessandro Biondi, Andrea Rovelli, Attilio Parini, Rossella