Thrombotic Microangiopathy Following Onasemnogene Abeparvovec for Spinal Muscular Atrophy: A Case Series
Titel:
Thrombotic Microangiopathy Following Onasemnogene Abeparvovec for Spinal Muscular Atrophy: A Case Series
Auteur:
Chand, Deepa H. Zaidman, Craig Arya, Kapil Millner, Rachel Farrar, Michelle A. Mackie, Fiona E. Goedeker, Natalie L. Dharnidharka, Vikas R. Dandamudi, Raja Reyna, Sandra P.