Quality of Life is Improved and Kidney Function Preserved in Patients with Nephropathic Cystinosis Treated for 2 Years with Delayed-Release Cysteamine Bitartrate
Titel:
Quality of Life is Improved and Kidney Function Preserved in Patients with Nephropathic Cystinosis Treated for 2 Years with Delayed-Release Cysteamine Bitartrate
Auteur:
Langman, Craig B. Greenbaum, Larry A. Grimm, Paul Sarwal, Minnie Niaudet, Patrick Deschenes, Georges Cornelissen, Elisabeth A.M. Morin, Denis Cochat, Pierre Elenberg, Ewa Hanna, Christian Gaillard, Segolene Bagger, Mary Jo Rioux, Patrice