Enzyme replacement therapy for mucopolysaccharidosis VI: A phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, open-label extension study
Titel:
Enzyme replacement therapy for mucopolysaccharidosis VI: A phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, open-label extension study
Auteur:
Harmatz, Paul Giugliani, Roberto Schwartz, Ida Guffon, Nathalie Teles, Elisa Leão Miranda, M. Clara Sá Wraith, J. Edmond Beck, Michael Arash, Laila Scarpa, Maurizio Yu, Zi-Fan Wittes, Janet Berger, Kenneth I. Newman, Mary S. Lowe, Ann M. Kakkis, Emil Swiedler, Stuart J.
Verschenen in:
Journal of pediatrics
Paginering:
Jaargang 148 (2006) nr. 4 pagina's 5.38999468E8 p.