Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human α-L-iduronidase (laronidase)
Titel:
Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human α-L-iduronidase (laronidase)
Auteur:
Wraith, James E Clarke, Lorne A Beck, Michael Kolodny, Edwin H Pastores, Gregory M Muenzer, Joseph Rapoport, David M Berger, Kenneth I Swiedler, Stuart J Kakkis, Emil D Braakman, Tanja Chadbourne, Elenie Walton-Bowen, Karen Cox, Gerald F