A different type of genetic therapy: correcting a defective gene using antisense oligonucleotide treatment in CEP290 p.Cys998X LCA
Titel:
A different type of genetic therapy: correcting a defective gene using antisense oligonucleotide treatment in CEP290 p.Cys998X LCA
Auteur:
Drack, Arlene V. Russell, Stephen R. Cideciyan, Artur V. Jacobson, Samuel G. Leroy, Bart P. Pfeifer, Wanda L. Dumitrescu, Alina V. Garafolo, Alexandra V. Ho, Allen C. Van Cauwenbergh, Caroline De Zaeytijd, Julie Hollander, Wil den Schwartz, Michael R. Asmus, Fredrich Girach, Aniz