Next generation triplex-forming PNAs for site-specific genome editing of the F508del CFTR mutation
Titel:
Next generation triplex-forming PNAs for site-specific genome editing of the F508del CFTR mutation
Auteur:
Gupta, Anisha Barone, Christina Quijano, Elias Piotrowski-Daspit, Alexandra S. Perera, J. Dinithi Riccardi, Adele Jamali, Haya Turchick, Audrey Zao, Weixi Saltzman, W. Mark Glazer, Peter M. Egan, Marie E.