Elexacaftor/tezacaftor/ivacaftor efficacy in intestinal organoids with rare CFTR variants in comparison to CFTR-F508del and CFTR-wild type controls
Titel:
Elexacaftor/tezacaftor/ivacaftor efficacy in intestinal organoids with rare CFTR variants in comparison to CFTR-F508del and CFTR-wild type controls
Auteur:
Kroes, Suzanne Bierlaagh, Marlou C. Lefferts, Juliet W. Boni, Alessandra Muilwijk, Danya Viscomi, Carla Keijzer-Nieuwenhuijze, Natascha D.A. Cristiani, Luca Niemöller, Paul J. Verburg, Tibo F. Cutrera, Renato Fiocchi, Alessandro G. Lucidi, Vincenzina van der Ent, Cornelis K. Beekman, Jeffrey M. Alghisi, Federico Ciciriello, Fabiana