Antisense oligonucleotide-based drug development for Cystic Fibrosis patients carrying the 3849+10 kb C-to-T splicing mutation
Titel:
Antisense oligonucleotide-based drug development for Cystic Fibrosis patients carrying the 3849+10 kb C-to-T splicing mutation
Auteur:
Oren, Yifat S. Irony-Tur Sinai, Michal Golec, Anita Barchad-Avitzur, Ofra Mutyam, Venkateshwar Li, Yao Hong, Jeong Ozeri-Galai, Efrat Hatton, Aurélie Leibson, Chen Carmel, Liran Reiter, Joel Sorscher, Eric J. Wilton, Steve D. Kerem, Eitan Rowe, Steven M. Sermet-Gaudelus, Isabelle Kerem, Batsheva