Efficacy and safety of ataluren in patients with nonsense-mutation cystic fibrosis not receiving chronic inhaled aminoglycosides: The international, randomized, double-blind, placebo-controlled Ataluren Confirmatory Trial in Cystic Fibrosis (ACT CF)
Titel:
Efficacy and safety of ataluren in patients with nonsense-mutation cystic fibrosis not receiving chronic inhaled aminoglycosides: The international, randomized, double-blind, placebo-controlled Ataluren Confirmatory Trial in Cystic Fibrosis (ACT CF)
Auteur:
Konstan, M.W. VanDevanter, D.R. Rowe, S.M. Wilschanski, M. Kerem, E. Sermet-Gaudelus, I. DiMango, E. Melotti, P. McIntosh, J. De Boeck, K.