2-Hydroxypropyl-β-cyclodextrin is the active component in a triple combination formulation for treatment of Niemann-Pick C1 disease
Titel:
2-Hydroxypropyl-β-cyclodextrin is the active component in a triple combination formulation for treatment of Niemann-Pick C1 disease
Auteur:
Davidson, Jessica Molitor, Elizabeth Moores, Samantha Gale, Sarah E. Subramanian, Kanagaraj Jiang, Xuntian Sidhu, Rohini Kell, Pamela Zhang, Jesse Fujiwara, Hideji Davidson, Cristin Helquist, Paul Melancon, Bruce J. Grigalunas, Michael Liu, Gang Salahi, Farbod Wiest, Olaf Xu, Xin Porter, Forbes D. Pipalia, Nina H. Cruz, Dana L. Holson, Edward B. Schaffer, Jean E. Walkley, Steven U. Maxfield, Frederick R. Ory, Daniel S.
Verschenen in:
Biochimica et Biophysica Acta. Molecular and cell biology of lipids