Toward responsible clinical n-of-1 strategies for rare diseases
Titel:
Toward responsible clinical n-of-1 strategies for rare diseases
Auteur:
Defelippe, Victoria M. J.M.W. van Thiel, Ghislaine Otte, Willem M. Schutgens, Roger E.G. Stunnenberg, Bas Cross, Helen J. O'Callaghan, Finbar De Giorgis, Valentina Jansen, Floor E. Perucca, Emilio Brilstra, Eva H. Braun, Kees P.J.