Nonclinical data supporting orphan medicinal product designations: lessons from rare neurological conditions
Titel:
Nonclinical data supporting orphan medicinal product designations: lessons from rare neurological conditions
Auteur:
Sheean, Maria E. Stoyanova-Beninska, Violeta Capovilla, Giuseppe Duarte, Dinah Hofer, Matthias P. Hoffmann, Michel Magrelli, Armando Mariz, Segundo Tsigkos, Stelios Shaili, Evyenia Polsinelli, Benedetta Ricciardi, Mario Bonelli, Milton Balabanov, Pavel Larsson, Kristina Sepodes, Bruno