Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Titel:
Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Auteur:
Mercuri, Eugenio Vilchez, Juan J Boespflug-Tanguy, Odile Zaidman, Craig M Mah, Jean K Goemans, Nathalie Müller-Felber, Wolfgang Niks, Erik H Schara-Schmidt, Ulrike Bertini, Enrico Comi, Giacomo P Mathews, Katherine D Servais, Laurent Vandenborne, Krista Johannsen, Jessika Messina, Sonia Spinty, Stefan McAdam, Laura Selby, Kathryn Byrne, Barry Laverty, Chamindra G Carroll, Kevin Zardi, Giulia Cazzaniga, Sara Coceani, Nicoletta Bettica, Paolo McDonald, Craig M