Safety and efficacy of cerliponase alfa in children with neuronal ceroid lipofuscinosis type 2 (CLN2 disease): an open-label extension study
Titel:
Safety and efficacy of cerliponase alfa in children with neuronal ceroid lipofuscinosis type 2 (CLN2 disease): an open-label extension study
Auteur:
Schulz, Angela Specchio, Nicola de los Reyes, Emily Gissen, Paul Nickel, Miriam Trivisano, Marina Aylward, Shawn C Chakrapani, Anupam Schwering, Christoph Wibbeler, Eva Westermann, Lena Marie Ballon, Douglas J Dyke, Jonathan P Cherukuri, Anu Bondade, Shailesh Slasor, Peter Cohen Pfeffer, Jessica