Safety and efficacy of leriglitazone for preventing disease progression in men with adrenomyeloneuropathy (ADVANCE): a randomised, double-blind, multi-centre, placebo-controlled phase 2–3 trial
Titel:
Safety and efficacy of leriglitazone for preventing disease progression in men with adrenomyeloneuropathy (ADVANCE): a randomised, double-blind, multi-centre, placebo-controlled phase 2–3 trial
Auteur:
Köhler, Wolfgang Engelen, Marc Eichler, Florian Lachmann, Robin Fatemi, Ali Sampson, Jacinda Salsano, Ettore Gamez, Josep Molnar, Maria Judit Pascual, Sílvia Rovira, Maria Vilà, Anna Pina, Guillem Martín-Ugarte, Itziar Mantilla, Adriana Pizcueta, Pilar Rodríguez-Pascau, Laura Traver, Estefania Vilalta, Anna Pascual, María Martinell, Marc Meya, Uwe Mochel, Fanny