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Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial |
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Titel: |
Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial |
Auteur: |
Masson, Riccardo Mazurkiewicz-Bełdzińska, Maria Rose, Kristy Servais, Laurent Xiong, Hui Zanoteli, Edmar Baranello, Giovanni Bruno, Claudio Day, John W Deconinck, Nicolas Klein, Andrea Mercuri, Eugenio Vlodavets, Dmitry Wang, Yi Dodman, Angela El-Khairi, Muna Gorni, Ksenija Jaber, Birgit Kletzl, Heidemarie Gaki, Eleni Fontoura, Paulo Darras, Basil T |
Verschenen in: |
The lancet neurology |
Paginering: |
Jaargang 21 () nr. 12 pagina's 1110-1119 |
Jaar: |
2022 |
Inhoud: |
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Uitgever: |
Elsevier Ltd |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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