Safety and efficacy of deferiprone for pantothenate kinase-associated neurodegeneration: a randomised, double-blind, controlled trial and an open-label extension study
Titel:
Safety and efficacy of deferiprone for pantothenate kinase-associated neurodegeneration: a randomised, double-blind, controlled trial and an open-label extension study
Auteur:
Klopstock, Thomas Tricta, Fernando Neumayr, Lynne Karin, Ivan Zorzi, Giovanna Fradette, Caroline Kmieć, Tomasz Büchner, Boriana Steele, Hannah E Horvath, Rita Chinnery, Patrick F Basu, Anna Küpper, Clemens Neuhofer, Christiane Kálmán, Bernadette Dušek, Petr Yapici, Zuhal Wilson, Ian Zhao, Feng Zibordi, Federica Nardocci, Nardo Aguilar, Christine Hayflick, Susan J Spino, Michael Blamire, Andrew M Hogarth, Penelope Vichinsky, Elliott