Safety and efficacy of olesoxime in patients with type 2 or non-ambulatory type 3 spinal muscular atrophy: a randomised, double-blind, placebo-controlled phase 2 trial
Titel:
Safety and efficacy of olesoxime in patients with type 2 or non-ambulatory type 3 spinal muscular atrophy: a randomised, double-blind, placebo-controlled phase 2 trial
Auteur:
Bertini, Enrico Dessaud, Eric Mercuri, Eugenio Muntoni, Francesco Kirschner, Janbernd Reid, Carol Lusakowska, Anna Comi, Giacomo P Cuisset, Jean-Marie Abitbol, Jean-Louis Scherrer, Bruno Ducray, Patricia Sanwald Buchbjerg, Jeppe Vianna, Eduardo van der Pol, W Ludo Vuillerot, Carole Blaettler, Thomas Fontoura, Paulo