Stakeholder collaboration for spinal muscular atrophy therapy development
Title:
Stakeholder collaboration for spinal muscular atrophy therapy development
Author:
Aartsma-Rus, Annemieke Balabanov, Pavel Binetti, Luca Haas, Manuel Haberkamp, Marion Mitchell, Joanna Rosa, Mário Miguel Muntoni, Francesco Finkel, Richard Mercuri, Eugenio