Oral cysteamine bitartrate and N-acetylcysteine for patients with infantile neuronal ceroid lipofuscinosis: a pilot study
Titel:
Oral cysteamine bitartrate and N-acetylcysteine for patients with infantile neuronal ceroid lipofuscinosis: a pilot study
Auteur:
Levin, Sondra W Baker, Eva H Zein, Wadih M Zhang, Zhongjian Quezado, Zenaide M N Miao, Ning Gropman, Andrea Griffin, Kurt J Bianconi, Simona Chandra, Goutam Khan, Omar I Caruso, Rafael C Liu, Aiyi Mukherjee, Anil B