Spinal presentations in children with spinal muscular atrophy type 1 following gene therapy treatment with onasemnogene abeparvovec – The SMA REACH UK network experience
Titel:
Spinal presentations in children with spinal muscular atrophy type 1 following gene therapy treatment with onasemnogene abeparvovec – The SMA REACH UK network experience
Auteur:
Wolfe, Amy Sheehan, Jennie Schofield, Alex Cranney, Helen O'Reilly, Emer Stimpson, Georgia Andrews, Alice Vanegas, Maria Lucas, Jonathan Scoto, Mariacristina Gowda, Vasantha Wraige, Elizabeth Jungbluth, Heinz