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Risk-benefit profile of onasemnogene abeparvovec in older and heavier children with spinal muscular atrophy type 1 |
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Titel: |
Risk-benefit profile of onasemnogene abeparvovec in older and heavier children with spinal muscular atrophy type 1 |
Auteur: |
Finnegan, Rebecca Manzur, Adnan Munot, Pinki Dhawan, Anil Murugan, Archana Majumdar, Anirban Wraige, Elizabeth Gowda, Vasantha Vanegas, Maria Main, Marion O'Reilly, Emer Baranello, Giovanni Muntoni, Francesco Scoto, Mariacristina |
Verschenen in: |
Neuromuscular disorders |
Paginering: |
Jaargang 42 () nr. C pagina's 22-26 |
Jaar: |
2024 |
Inhoud: |
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Uitgever: |
Elsevier B.V. |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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