O.06 Long term outcomes for X-Linked myotubular Myopathy (XLMTM) with gene replacement therapy, resamirigene bilparvovec: Preliminary results from ASPIRO
Titel:
O.06 Long term outcomes for X-Linked myotubular Myopathy (XLMTM) with gene replacement therapy, resamirigene bilparvovec: Preliminary results from ASPIRO
Auteur:
Shieh, P. Kuntz, N. Dowling, J. Müller-Felber, W. Blaschek, A. Bönnemann, C. Foley, R. Saade, D. Seferian, A. Servais, L. Bowden, A. Sarazen, M. Coats, J. Lakshman, N. Han, C. Prasad, S. Rico, S. Miller, W.