O.10 First-in-human intrathecal gene transfer study for giant axonal neuropathy: Preliminary review of long-term efficacy and safety
Titel:
O.10 First-in-human intrathecal gene transfer study for giant axonal neuropathy: Preliminary review of long-term efficacy and safety
Auteur:
Bharucha-Goebel, D. Saade, D. Todd, J. Norato, G. Jain, M. Waite, M. Armao, D. Foley, A. Lehky, T. Averion, G. Hu, Y. Mohassel, P. Hoke, A. DeLong, T. Acquaye, N. Hinkley, L. Chichester, J. Mendoza, C. Soldatos, A. Gray, S. Bönnemann, C.