FP.17 Long-term follow-up of cipaglucosidase alfa/miglustat in ambulatory patients with Pompe disease: An open-label phase I/II study (ATB200-02)
Titel:
FP.17 Long-term follow-up of cipaglucosidase alfa/miglustat in ambulatory patients with Pompe disease: An open-label phase I/II study (ATB200-02)
Auteur:
Schoser, B. Kishnani, P. Bratkovic, D. Clemens, P. Goker-Alpan, O. Ming, X. Roberts, M. Vorgerd, M. Sivakumar, K. van der Ploeg, A. Goldman, M. Wright, J. Holdbrook, F. Jain, V. Sitaraman, S. Wasfi, Y. Mozaffar, T. Byrne, B.