P.126 Genotype-unmatched controls are feasible for drug development in Duchenne muscular dystrophy (DMD)
Title:
P.126 Genotype-unmatched controls are feasible for drug development in Duchenne muscular dystrophy (DMD)
Author:
Muntoni, F. Signorovitch, J. Frean, M. Fillbrunn, M. Sajeev, G. Ward, S. McDonald, C. Goemans, N. Niks, E. Wong, B. Servais, L. Straub, V. de Groot, I. Chesshyre, M. Tian, C. Manzur, A. Mercuri, E. Aartsma-Rus, A. Groups, Study